The first patient to undergo recently approved gene therapy for sickle cell disease, Kendric Cromer, has left the hospital.

After 44 days, Kendric Cromer, 12, left the hospital. While his family feels fortunate that he was the first to receive a treatment, their difficult experiences hint at what others will be up against.

Kendric Cromer began treatment with Bluebird bio's sickle cell gene therapy in May. Physicians removed stem cells from his bone marrow and sent them to a facility where new, healthy hemoglobin genes ...

Kamala Harris hit the road today for campaign events in the three battleground states that make up her clearest possible path ...

Sep. 25, 2024 — Adults with hemophilia B saw their number of bleeding episodes drop by an average of 71 percent after a single infusion of gene therapy, according to the new results of an ...

Gene therapy could help obese kids avoid health problems associated with excess weight, including arthritis, a new, preliminary study in mice suggests. The gene therapy prompts cells to convert ...

Gene Therapy with Fidanacogene Elaparvovec in Adults with Hemophilia B. New England Journal of Medicine , 2024; 391 (12): 1108 DOI: 10.1056/NEJMoa2302982 Cite This Page : ...

UK-headquartered Beacon Therapeutics has raised a whopping $170 million in second-round financing that will be used to advance a gene therapy for an inherited cause of blindness through a pivotal ...

A new gene therapy approved earlier this year can serve as a sustainable single-dose treatment for people with hemophilia B, newly published clinical trial data shows. People with hemophilia B saw ...

Gene therapy holds promise for treating some of these conditions, and current research advances may soon shift the therapeutic landscape for eye health. However, many obstacles remain in place ...

Fidanacogene elaparvovec, an adeno-associated virus (AAV) gene-therapy vector for hemophilia B containing a high-activity human factor IX variant (FIX-R338L/FIX-Padua), was associated with ...

Chief Justice of India D Y Chandrachud stressed the importance of making costly gene therapy accessible to all, especially those outside urban centers. Speaking at a Bengaluru conference ...